[HN Gopher] Cure ID App Lets Clinicians Report Novel Uses of Exi...
       ___________________________________________________________________
        
       Cure ID App Lets Clinicians Report Novel Uses of Existing Drugs
        
       Author : throw0101d
       Score  : 56 points
       Date   : 2025-04-10 22:34 UTC (4 days ago)
        
 (HTM) web link (www.fda.gov)
 (TXT) w3m dump (www.fda.gov)
        
       | mdip wrote:
       | Interesting ... it's presented in the context of drugs for curing
       | infections.
       | 
       | I wonder if this is being used for other drugs. My curiosity
       | stems from personal experience: I had Migraine headaches from age
       | 17 to about 35. I was put on ancient seizure medication that's
       | common prescribed for Bipolar[0] because this doctor had three
       | other patients that it nearly eliminated Migraine from. It was
       | fall, a time when I'd get about one a week. After five days of
       | taking it, I had my first Migraine ... if you could call it that
       | -- I could only identify that it _was_ a Migraine by the aura;
       | the pain was about 10% what I 'm used to).
       | 
       | Searching through the web, I found a forum that was filled with
       | Migraine sufferers. Sure enough, there were a handful of people
       | who _swore_ by it. There were also a handful of people who it
       | didn 't work for. Looking at the more official sources, there was
       | no indication that this drug could have _any_ effect on Migraine;
       | they listed all of the _other_ off-label uses[1], but Migraine
       | was not among them.
       | 
       | This medication had been in the news several times (and on the
       | front page, here[2]) over the last few years and a year ago (or
       | so), I looked it up on the "official sources", again. It now
       | indicated that it was prescribed for Migraine.
       | 
       | It made me wonder ... how are things like that figured
       | out/communicated down-stream? Is it entirely informally amongst
       | doctors? I went to four different specialists before I found one
       | who suggested this drug -- and he did so in a "half-hearted
       | manner" not truly expecting it would work. It'd be nice if this
       | was centrally tracked/managed as it might surface both "new uses
       | for old drugs" and "new problems with old drugs."
       | 
       | [0] Which I do not have.
       | 
       | [1] It's rarely, if ever, prescribed for what it was originally
       | approved for.
       | 
       | [2] It's Depakote, I'm not being cagey for nefarious purposes, I
       | just didn't want this to be a drug advertisement.
        
         | meew0 wrote:
         | Once drugs lose patent protection, it's difficult for them to
         | gain approval for new indications, because drug approval
         | procedures are extremely expensive and there's no patent holder
         | left for whom it would make economic sense to spend all that
         | money.
         | 
         | So in cases like valproate for migraine, those drugs usually
         | stay off-label long term. That makes them unattractive for
         | doctors to prescribe, since they assume more liability if
         | something goes wrong, and insurance companies are less likely
         | to cover the drugs.
         | 
         | The way information about off-label uses gets communicated is
         | basically the same way as elsewhere in science: through
         | scientific papers, conferences, textbooks, and the like. A
         | doctor who discovers that their migraine patient does well on
         | valproate might publish this as a case report. If there are
         | many such reports, someone might do a randomized trial. Once
         | there are many randomized trials, meta-analyses can be
         | performed, and eventually, the information will end up in
         | textbooks and medical school curricula.
         | 
         | It takes a certain amount of agency for a doctor to stay up to
         | date on the latest research; while medical boards tend to have
         | certification requirements for CME (continuing medical
         | education), these are usually quite lax, and a truly lazy
         | doctor can probably just live their years without really
         | learning anything new.
         | 
         | At the same time, reading all new research that comes out is
         | basically impossible, and even just trying to do this would
         | risk always following the latest fads that later evidence might
         | show to, in fact, be harmful. Every doctor needs to find their
         | own middle ground here, and you as a patient must find a doctor
         | that suits your own preferences.
        
           | smeej wrote:
           | I wonder if some sort of coalition of compounding pharmacists
           | might be up for making and retaining a repository. They at
           | least make _some_ money by helping would-be patients take
           | these drugs, right? So even if it 's nothing like Big Pharma
           | money, I can't really think of anybody who'd have a better
           | chance to benefit from promoting off-label use cases for out
           | of patent drugs than them.
        
           | dylan604 wrote:
           | > Once drugs lose patent protection, it's difficult for them
           | to gain approval for new indications, because drug approval
           | procedures are extremely expensive and there's no patent
           | holder left for whom it would make economic sense to spend
           | all that money.
           | 
           | This is precisely why I think a gov't run research effort is
           | the right way to handle this. You don't want to grant a new
           | patent on the existing drug just because of new use of it.
           | That would prevent the generics being used for the original
           | purpose. So if the bigPharma company that created it for
           | original purposes does not want to spend money researching
           | alternate uses, then allow the gov't direct the research in
           | the name of keeping its citizens healthy.
           | 
           | Unfortunately, that doesn't really stand up as a great
           | solution with using the current administration as an example
           | of what happens when you get anti-science mindsets in charge
           | of things. It also helps to have a gov't that is empathetic
           | for its citizens which does not always happen.
        
             | meew0 wrote:
             | Yes, in fact, most of the types of research I mentioned,
             | where random people at hospitals do small trials on
             | existing medications, is going to be partially government
             | funded.
             | 
             | But care must be taken to avoid the tulip subsidies problem
             | [1]: the barriers to drug approval are regulatory, not
             | natural. If a drug regulatory agency sets high requirements
             | for approval and another governmental agency must do
             | expensive work to satisfy these requirements, there is a
             | risk that costs go out of control without any real benefit.
             | 
             | Instead, my favoured solution would be to significantly
             | relax regulatory requirements in cases like this where a
             | drug has already been proven to be safe both in the
             | original approval trials and in years of real-world use,
             | such that when trials and meta-analyses exist that suffice
             | to convince the medical establishment of a drug's safety
             | and efficacy for a new indication, these would also be
             | enough for the drug to gain approval for that indication.
             | 
             | [1] https://slatestarcodex.com/2015/06/06/against-tulip-
             | subsidie...
        
         | LorenPechtel wrote:
         | Yeah, sounds like they got something right.
         | 
         | Real world, sometimes a doctor will think up a novel use of the
         | effect of a drug. And sometimes they'll throw stuff at the wall
         | and see what sticks. When you don't have a good answer this can
         | be sane medical practice. But there should be a requirement of
         | reporting it to something like this database.
        
         | GuinansEyebrows wrote:
         | I'm in the same boat with propanalol - my doctor told me it was
         | "the worst blood pressure medication available, but
         | surprisingly effective at preventing migraine symptoms (as well
         | as physical symptoms of anxiety)".
        
       | navan wrote:
       | Just today I read about this in the book "Who is Government" by
       | Michael Lewis where he presents the case on how it can help find
       | cure for rare diseases. You can read his article at
       | https://www.washingtonpost.com/opinions/interactive/2025/mic....
       | 
       | Also highly recommend the book.
        
         | rvba wrote:
         | That article has a horrible writing style. So much fluff and so
         | litlle content.
        
       | adamredwoods wrote:
       | I wonder how this is going (started 2013), because I have a hunch
       | it will be chasing ghosts, mostly. Placebo affect is a factor
       | here. I also wonder how many fake leads from "propaganda
       | physicians" they get.
        
         | bluGill wrote:
         | The real thing is can we (perhaps with new advances in
         | statistics?) find places where doctors at the end of all known
         | treatment try things at random and see if anything works. For
         | rare symptoms it often isn't possible to run a proper
         | controlled study (note that I said symptoms and not disease -
         | often we are not really sure what is going on). So if we can
         | give doctors a list "here is what someone else tried and or
         | treatment Y seems to make things worse that is a clue.
         | Eventually we can say that we don't know why, but X seems like
         | your best shot even if it we can never get to real statistical
         | significance.
         | 
         | Doctors already have case studies which they (at least should)
         | publish anytime they get someone who for whatever reason
         | doesn't respond to standard treatment, or has something
         | unknown. However it is hard for the next doctor to find any
         | that might be relevant.
        
         | lenerdenator wrote:
         | You don't know you're chasing ghosts until you start running.
         | 
         | There's not much wrong with the system so long as it's used as
         | a place to get ideas for clinical studies or absolute last-
         | ditch attempts at saving lives. On occasion (like the Milwaukee
         | Protocol for rabies), those last-ditch attempts do work.
         | 
         | It's when people pretend there's no real investigation to be
         | done that we get problems.
        
         | GuinansEyebrows wrote:
         | Yeah, this seems like a worthwhile service, but I can't stop
         | thinking about ivermectin.
        
           | mschuster91 wrote:
           | It became apparent really fast that ivermectin was
           | effective... against a superinfection with parasites, which
           | the reported success cases all had.
           | 
           | But by the time it became apparent, the correction didn't
           | spread nearly as fast nor wide as the original information.
           | 
           | The problem is, most people lack the scientific literacy to
           | understand how science works, and many newspapers have long
           | since gutted their expert journalists.
        
       | jjtheblunt wrote:
       | "Content current as of: 06/08/2020"
        
       | CharlieDigital wrote:
       | Very cool seeing this show up on HN. FDA has a bunch of
       | interested datasets like this that are full of interesting data
       | points.
       | 
       | During COVID, I actually wrote a small sample app that pulls info
       | from this DB: https://www.covidcureid.com/
       | 
       | And gave a talk on it: https://learn.microsoft.com/en-
       | us/shows/azure-serverless-con...
        
         | radicalbyte wrote:
         | How viable would it be to mirror the set? Given that the US is
         | having it's ISIS book-burning moment so the original sources
         | are at risk :(
        
           | CharlieDigital wrote:
           | Try emailing the team and see if you can get the data set:
           | https://cure.ncats.io/resources/ehr-resources
           | 
           | Otherwise, my code to extract the data is here: https://githu
           | b.com/CharlieDigital/covidcureid/blob/main/serv...
        
             | Onawa wrote:
             | NCATS and other NIH data resource teams were heavily
             | affected or completely dismantled during the latest
             | reductions in force (RIFs). Getting data from certain areas
             | inside HHS will be difficult to impossible for the
             | foreseeable future.
        
           | kens wrote:
           | Your concerns may be justified. The site says: "This
           | repository is under review for potential modification in
           | compliance with Administration directives."
        
       ___________________________________________________________________
       (page generated 2025-04-14 23:01 UTC)