[HN Gopher] What is metformin's secret sauce?
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       What is metformin's secret sauce?
        
       Author : XzetaU8
       Score  : 65 points
       Date   : 2024-12-18 20:43 UTC (2 hours ago)
        
 (HTM) web link (news.northwestern.edu)
 (TXT) w3m dump (news.northwestern.edu)
        
       | vlod wrote:
       | FTA: "But until now, scientists have been unable to determine
       | how, exactly, the drug works."
       | 
       | Try that next time you submit a PR: Yeah... it works, but "I am
       | unable to determine how exactly".
       | 
       | I find this concept absolutely mind blowing. We take drugs that
       | the creators of the drugs don't understand how they work.
       | 
       | I realize that biology is hard to understand, but this sounds
       | crazy.
        
         | Trasmatta wrote:
         | That's very common actually! The mechanism of action for many
         | drugs is unknown. And then it gets even weirder with
         | psychoactive drugs: eventually the answer is "this drug effects
         | this neurotransmitter which gives you this subjective first
         | person experience, and we don't really know why". It brings up
         | a lot of philosophical and existential questions!
        
           | lordnacho wrote:
           | How do people come to find these drugs then? If you don't
           | have a theory about how something works, what would make you
           | test whether it works?
        
             | MaxDPS wrote:
             | Sometimes there is a theory, but it's also possible for a
             | drug to help in other (unrelated) ways as well.
        
             | pitpatagain wrote:
             | In the case of metformin, the direct line is from guanidine
             | in french lilac being used since the middle ages for
             | diabetes. Guanidine is effective, but long term liver
             | toxic.
             | 
             | Once actual chemistry broke open our ability to analyze
             | that drug, related chemicals could be synthesized and
             | studied, which led to biguanidines, of which metformin is
             | one, which were tested in animals.
             | 
             | Many drugs are found this way by looking at chemicals
             | related to ones we already know about, and then testing on
             | animals and humans. Self testing of new drugs by
             | researchers used to be very common.
             | 
             | How did folk medicine come to know the effects of
             | guanidine? Dunno.
        
               | groby_b wrote:
               | > How did folk medicine come to know the effects of
               | guanidine? Dunno.
               | 
               | The same way we know a lot about other things in the
               | chemistry domain - somebody tasted it, just to see what
               | happens. "Mendeleyev's Dream" is a great book that
               | contains many fascinating anecdotes of people going "let
               | me just lick this, just to try". (Or, if you want to go
               | more modern, the history of hallucinogens is pretty fun
               | too)
               | 
               | Humans seem to have a strong tendency to stuff unknown
               | things into their mouth, just because they can.
        
               | falcor84 wrote:
               | Indeed. I would assume that this is one of the traits
               | that survives due to group selection [0] - it would be
               | bad if everyone in the population was such a risk taker,
               | but groups that have a small percentage of these people
               | will adapt better.
               | 
               | [0] https://en.wikipedia.org/wiki/Group_selection
        
             | hmottestad wrote:
             | I think it's more often <<we know that this drug lowers X
             | in blood results, cause we saw that when we trialed it for
             | something a few years ago that didn't work out, now we've
             | found out that disease B shows high values of X...>>
        
             | robocat wrote:
             | A fabulous book on this is Phenethylamines I Have Known and
             | Loved (PiHKAL) which can be found as a PDF online (the link
             | I had has died but try Google and filetype:pdf).
             | 
             | Summary: a chemist is interested in psychedelics so he
             | starts creating candidate psychoactive substances, and he
             | then tests them on himself and friends. He wrote a lovely
             | book about his journey.
        
             | a_wild_dandan wrote:
             | Expected utility, just like anything else. It's why our
             | ancestors ate willow tree bark (aspirin), for instance.
        
             | sjducb wrote:
             | Mostly enormous libraries of compounds.
             | 
             | You take a cell culture model for the disease and see if
             | the compounds affect the cells.
             | 
             | Then try it in animals, then humans.
             | 
             | Repeat this process until you have good safe drugs for all
             | of the diseases.
        
             | mtlmtlmtlmtl wrote:
             | Sometimes by accident. The original serotonergic
             | antidepressants were antibiotics that happened to have MAO
             | inhibition as a side effect. Initially developed to treat
             | tuberculosis, doctors noticed the drugs had a stimulating
             | side effect. A year later, a psychiatrist decided to trial
             | them for depression, and found some success.
             | 
             | It's actually the other way around. They didn't have very
             | serious theories about the etiology of depression back
             | then, the only clue they had was from the pharmacology of
             | these drugs, which led to the situation where for many
             | years the leading theory on depression was that it was
             | caused by low levels of monoamine
             | neurotransmitters(serotonin, norepinephrine and dopamine).
             | The main evidence for this initially was the fact that
             | these drugs seemed to work, and that they increased the
             | levels or effects of monoamines. This theory has since
             | become discredited as we've learned more, although the
             | connection between monoamines and depression is still
             | strong. It's just not the whole picture.
        
         | profunctor wrote:
         | If your pr deploys a machine learning model then that would be
         | a suitable comment. I suppose the idea is similar, we can
         | determine that this drug helps so a (hopefully) statistically
         | significant degree so even if we don't know how it works we
         | want to use it.
        
         | renewiltord wrote:
         | Does it sound crazy? Most startups don't understand _why_ their
         | product gains traction. They have less comprehension by this
         | standard than the scientists with drugs. One of the beautiful
         | things about knowledge is this: you don't need knowledge of
         | components to know the whole.
        
           | vlod wrote:
           | Sure. However the implications if your stupid sass app [0]
           | fails or not is not in the same league (IMHO) as messing with
           | humans biology.
           | 
           | [0]: Yes there may be medical sass apps that are more serious
        
         | justinko wrote:
         | Sorry bro, human biology is infinitely more complex than your
         | CRUD app.
        
           | vlod wrote:
           | Oh... I agree.. I'm just shocked at the attitude.
           | 
           | i.e. "We don't quite know how it works... but statistically
           | we think it will help, with these side-effects.. good luck"
           | <gasp>
        
             | glial wrote:
             | Yes, I remember learning about this issue with psychiatric
             | medications and being similarly dismayed.
             | 
             | There is a sub-field called Computational Psychiatry [1]
             | trying to do better. And interestingly, a person could
             | argue that randomized controlled trials for medicine are
             | only really necessary because we _don 't_ have good enough
             | theory and/or good enough measurement devices. If we did,
             | we could reliably predict the effects of a medication
             | without the trial.
             | 
             | [1] https://www.nature.com/articles/nn.4238
        
         | mft_ wrote:
         | The process for approving a new drug essentially requires
         | proving that they are safe and also have sufficient efficacy,
         | and usually also that the balance of the two (aka benefit:risk)
         | is an improvement over a reasonable existing comparator.
         | 
         | There are plenty of drugs I can think of (even relatively
         | modern, specialised drugs) for which we kinda understand some
         | parts of the mechanism of action, but not other parts.
         | 
         | Also, given how difficult and competitive developing new drugs
         | is, the incentive is to do the minimum (as above) for approval
         | in the shortest time possible.
        
         | aftbit wrote:
         | I've submitted just such PRs before, usually with a comment
         | along the line of "this hack is dumb and I do not yet
         | understand why it is necessary, but it works now, tests prove
         | it works, and I have more urgent things to do." Sometimes this
         | is unacceptable but often it is just what the doctor ordered.
         | 
         | Of course, unlike with biology, it is usually not beyond my
         | skills to eventually understand the whole system, but it may be
         | beyond my time availability. With biology, the whole thing is
         | just too complex to grok.
        
           | falcor84 wrote:
           | Reminds me of the classic story about the 'more magic' switch
           | - http://catb.org/jargon/html/magic-story.html
        
         | inglor_cz wrote:
         | Biology is a result of billions of years of constant
         | evolutionary struggle on a planetary scale, without rhyme or
         | reason, very much _not_ intelligently designed. Whatever random
         | mutation worked, worked.
         | 
         | We the IT people love to complain about esoteric interplay of
         | hardware, OS, apps and network. There is a lot _more_ phenomena
         | in constant interplay even in mere amoebas, not to speak of
         | human bodies.
         | 
         | Not to mention that you just cannot put breakpoints into a
         | living organism and read its current status on screen.
         | 
         | I find it positively crazy that we know something about biology
         | at all. The intrinsic obstacles are just so much higher than in
         | software.
        
         | aftbit wrote:
         | What's the alternative? Never develop or deliver a life-
         | improving medication until we can fully understand it from
         | first principles? Gonna be waiting a long time IMO.
        
         | pedalpete wrote:
         | It's the same with neurology. We pretend we understand how the
         | brain works, but much of what we are understanding is our
         | current conceptual knowledge, so it's theoretical.
         | 
         | We work with Phase-targeted auditory stimulation to enhance
         | deep sleep (https://affectablesleep.com). We know we can
         | stimulate the brain during sleep and measure the increase in
         | electrical activity which is the result of increased
         | synchronous firing of neurons, but the reason why we are able
         | to create this result is just a theory. However, the behaviour
         | itself is consistent, and replicated.
        
         | xkcd-sucks wrote:
         | It's completely rational just inverted -- Our understanding of
         | biology is based on testing hypotheses of how drugs work,
         | mostly. Some of the best practical understanding comes from
         | "phase 4 clinical trials" i.e. those performed informally by
         | the market
        
         | tippytippytango wrote:
         | Evolution just pushes straight to master.
        
           | falcor84 wrote:
           | But with a very gradual rollout, with automatic rollback
        
         | groby_b wrote:
         | Welcome to medicine and biology. We have no idea how a lot of
         | stuff works (ask an anesthesiologist how anesthesia actually
         | works, if you don't mind being freaked out). We just know it
         | seems to reliably work.
         | 
         | This extends all the way to surgical procedures, which often
         | amount to "should fix your issues, IDK" especially when it
         | comes to soft tissue.
         | 
         | I like to think of it as a stochastic discipline. (Which means
         | that you want doctors who understand probabilities. Many don't.
         | Filter well)
        
         | marcellus23 wrote:
         | Tell me you've never worked on a huge production codebase
         | without telling me you've never worked on a huge production
         | codebase. Sometimes you need to fix a problem and you just
         | don't have days to spend finding out the root cause.
        
         | devilbunny wrote:
         | We have some clues but not much real, deep understanding of how
         | general anesthetics work. Process that for a second.
         | 
         | They've been in use since at least the early 19th century. We
         | have had a bunch of them (though in humans, at least, we pretty
         | much only use 4 or 5 in developed countries these days). We do
         | this every day in surgical suites around the world. People
         | _expect_ to be unconscious during surgery. But we don 't really
         | know _how_ they do it.
         | 
         | Or take antipsychotics: the companies were looking for
         | antihistamines and noticed psychotic patients got better on
         | some of them. If it works... you keep using it until something
         | better shows up.
        
       | throw4321 wrote:
       | The article mentions Metformin's use in preventing Long Covid.
       | More info on that from Eric Topol's blog:
       | https://erictopol.substack.com/p/preventing-long-covid
       | 
       | The original study:
       | https://papers.ssrn.com/sol3/papers.cfm?abstract_id=4375620
        
       | Alex3917 wrote:
       | > metformin blocks a specific part of the cell's energy-making
       | machinery called mitochondrial complex
       | 
       | Keep in mind that any mitochondrial complex I inhibitor that is
       | sufficiently strong is going to cause PSP if you take it for long
       | enough, which is basically a fatal and untreatable version of
       | Parkinson's disease. I haven't seen much research on this being a
       | risk specifically for metformin, but I'd be careful about trying
       | to use it prophylactically for longevity purposes rather than for
       | a specific medical condition.
        
         | klipklop wrote:
         | Very interesting. I wonder if there is any study/evidence
         | indicating PSP can happen to somebody taking metformin that
         | does _not_ have T2D.
        
         | teej wrote:
         | Source?
         | 
         | Metformin is one of the most widely studied drugs on the
         | market. I can't find any study that links it to PSP
         | (Progressive Supranuclear Palsy).
        
           | Alex3917 wrote:
           | There aren't any papers that I know of on metformin and PSP,
           | but there are lots of papers on rotenone/acetogenins and PSP.
        
         | radicaldreamer wrote:
         | This seems unlikely but possible. Metformin is widely
         | prescribed worldwide and as far as I know, no correlation has
         | been shown. Granted, what its prescribed for - diabetes and
         | prediabetes - are themselves risk factors for neurodegenerative
         | diseases.
        
         | tomlue wrote:
         | This comment may unnecessarily discourage people from using
         | metformin.
         | 
         | - There is no evidence linking metformin to PSP, let alone a
         | causal relationship. - PSP is also very rare, prevalence ~ 7
         | per 100,000 [1]. - Metformin is used by 100+ million people
         | [2]. - It has been safely prescribed for type 2 diabetes since
         | the late 1950s [2].
         | 
         | Metformin is a highly effective and widely used medication. It
         | would be unfortunate for people to avoid it based on
         | speculative claims. If there's specific evidence suggesting
         | metformin as a risk factor for PSP, I'd be interested, but the
         | leap from "mitochondrial complex I inhibition is associated
         | with PSP" to "metformin causes PSP" is unwarranted.
         | 
         | As for the prophylactic use comment: we are all going to decay
         | and die, trying to mitigate those risks with metformin is not
         | unreasonable. There is evidence supporting its potential
         | benefits, though some of these may reflect its established role
         | in managing diabetes. (talk to your doctor, etc.)
         | 
         | [1]
         | https://link.springer.com/article/10.1007/s00415-023-11791-2
         | [2]
         | https://www.metabolismjournal.com/article/S0026-0495%2822%29...
        
           | Alex3917 wrote:
           | > the leap from "mitochondrial complex I inhibition is
           | associated with PSP" to "metformin causes PSP" is unwarranted
           | 
           | The mechanism of action is relatively straightforward: the
           | inhibition is caused by a building up oxides within the
           | mitochondria, which makes them less efficient at producing
           | energy. And if the mitochondria go long enough without a
           | mitochondrial antioxidant clearing out the oxides, they
           | eventually die. And if enough of the mitochondria within your
           | brain die, you get PSP.
           | 
           | My best guess as to the reason we haven't seen an association
           | between PSP and metformin is that metformin is actually a
           | mitochondrial type I adaptogen rather than a mitochondrial
           | type I inhibitor. I'm definitely not telling people not to
           | take it, but if you are then I think setting a couple Google
           | scholar alerts would be prudent.
        
       | jonplackett wrote:
       | I don't get it. Why would decreasing the function of mitochondria
       | be a good thing? Can anyone explain?
        
         | klipklop wrote:
         | It would indeed be bad if it was systemic. The link seems to
         | suggest it's only certain cells that have influence over blood
         | sugar (the gut, liver, etc).
        
           | fellowmartian wrote:
           | An alternative explanation would be that creates
           | mitochondrial stress that is in beneficial in some ways,
           | maybe similar to Zone 2 training?
        
         | dinfinity wrote:
         | I also did not understand why it would lower blood glucose, but
         | that is due to my lack of understanding cells. I asked some
         | help from ChatGPT and got this info:
         | 
         | "Inhibiting a mitochondrial complex (e.g. one of the electron
         | transport chain complexes) would decrease a cell's ability to
         | generate ATP through oxidative phosphorylation. As a result,
         | cells would rely more heavily on glycolysis to meet their
         | energy needs, which increases their consumption of glucose.
         | This heightened glycolytic flux leads to higher glucose uptake
         | from the bloodstream and a corresponding drop in blood glucose
         | levels.
         | 
         | [...]
         | 
         | Cells generally prefer using oxidative phosphorylation (the
         | mitochondrial pathway) over glycolysis to generate ATP because
         | it is more energy-efficient. Oxidative phosphorylation can
         | produce around 30-36 ATP per glucose molecule, while glycolysis
         | alone only nets about 2 ATP per glucose."
         | 
         | (Standard disclaimers as to LLM hallucinations apply)
        
           | garganzol wrote:
           | > "This heightened glycolytic flux leads to higher glucose
           | uptake"
           | 
           | This is a dubious statement. While glycolysis indeed consumes
           | glucose, the amount of that consumption is expected to be
           | significantly lower than through oxidative phosphorylation.
           | 
           | For example, if you deprive cells from oxygen, oxidative
           | phosphorylation gets inhibited and glycolysis kicks in as an
           | alternative metabolic pathway. As a result, blood glucose
           | level goes through the roof. This is what can be seen in
           | patients with acute respiratory distress syndrome.
           | 
           | But it is more complicated than that - when oxygen level
           | drops, the nervous system starts gluconeogenesis as an
           | attempt to compensate for the lack of oxygen by increasing
           | the levels of glucose in the bloodstream. So we have multiple
           | parallel effects going on: lower glucose consumption by
           | oxidative phosphorylation due to the lack of oxygen + higher
           | glucose consumption by glycolysis + higher glucose injection
           | via gluconeogenesis. The net result of that formula is that
           | blood glucose level goes up for almost all patients with
           | hypoxemia.
           | 
           | Still, glycolysis alone cannot explain the effect of
           | metformin. If it was really a glycolysis with such an
           | amplitude caused by metformin intake, people would start to
           | develop lactic acidosis, air hunger, cellular damages,
           | neuropathy, dementia, cancer.
           | 
           | Honestly speaking, the only viable explanation so far is that
           | metformin may cause mitochondria training by mildly and
           | temporary putting a strain on ETC. Like a mild physical
           | activity would do. Anything more impactful than "mild" would
           | lead to an excessive oxidative stress, cellular damages, air
           | hunger, suffocation, and tons of dangerous consequences.
        
         | byyoung3 wrote:
         | cells can only divide so many times.
        
         | nonameiguess wrote:
         | Sounds like it's exactly the same "magic" as exercise and
         | calorie restriction. If the body has more energy available than
         | it needs for normal function, it'll use as much as it can and
         | eventually that use goes to things like general inflammation,
         | cancer, and autoimmune disease. If you use available energy to
         | exercise, simply eat less, or disrupt your body's ability to
         | actually use all the excess food you feed it with drugs, then
         | it won't be able to do those bad things and will only maintain
         | essential function.
         | 
         | Obviously, if you restrict too much, you starve. Animals in a
         | state of nature seem to automatically find the right balance
         | and eat roughly exactly what they need. Animals placed into
         | situations in which food is nearly costless, effectively
         | infinite, and you don't need to be active except to the extent
         | you do it freely for recreation, seem to struggle. Humans
         | suffering from diseases of civilization are one such example,
         | but human pets and livestock seem to have the same problems.
         | Presumably, lab rats are basically like that, too. Life in a
         | plastic cage with no predators and food given to you directly
         | by gods is not very similar to life in the wild.
        
       | epmatsw wrote:
       | Re: longevity, ITP didn't find any significant impact from
       | metformin. Afaik they're the most rigorous testers of this sort
       | of thing, so that's pretty significant to me.
       | 
       | https://pubmed.ncbi.nlm.nih.gov/27312235/
        
         | klipklop wrote:
         | ...in mice.
         | 
         | Also.
         | 
         | >Metformin (0.1%) combined with rapamycin (14 ppm) robustly
         | extended lifespan, suggestive of an added benefit, based on
         | historical comparison with earlier studies of rapamycin given
         | alone.
        
         | ziddoap wrote:
         | > _ITP_
         | 
         | Interventions Testing Program (by The National Institute on
         | Aging) for the unfamiliar, like me.
        
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