[HN Gopher] Genetic repair via CRISPR can inadvertently introduc...
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       Genetic repair via CRISPR can inadvertently introduce other defects
        
       Author : amichail
       Score  : 87 points
       Date   : 2024-11-08 17:13 UTC (5 hours ago)
        
 (HTM) web link (phys.org)
 (TXT) w3m dump (phys.org)
        
       | psadri wrote:
       | Let's say you have a running program on a computer, and you
       | figure out a way to swap out parts of its instructions / state in
       | RAM while it is running. What are the odds of your swap causing
       | problems? Now, what if the program is 100 - 1000x more complex
       | than anything you have ever managed to create.
        
         | georgyo wrote:
         | You may not remember GameSharks, but those things did you
         | exactly what you suggest. As do most game cheat engines.
         | Editing the state, directly in RAM, without the program's
         | knowledge.
         | 
         | The next time something tries to use whatever memory or
         | function it overroad, it would pick up your version instead.
        
           | 0x457 wrote:
           | I think this is more like introducing and RCE into your body,
           | since CRISPR essentially modifies your executable code?
        
             | thrw42A8N wrote:
             | DNA is more like configuration for your molecural
             | factories.
        
               | exe34 wrote:
               | configuration is code.
        
               | 0x457 wrote:
               | speakig like a true "exe"
        
               | thrw42A8N wrote:
               | Not in this case. There is only a very restricted set of
               | options and these can be interpreted in different ways by
               | different machines that read it.
        
           | hoherd wrote:
           | FYI doing this to a game is illegal in Japan, which kinda
           | makes it seem like CRISPR should also be illegal in Japan.
        
           | chiffre01 wrote:
           | I remember having a Game Genie, it worked sometimes. But like
           | the article says. it would also make things glitchy and crash
           | everything now and then.
        
             | jncfhnb wrote:
             | Not surprising. They weren't designed cheat codes. Folks
             | would try stuff, sort of figure out what it did, and then
             | publish it with a name.
        
         | TrainedMonkey wrote:
         | Biology is already probabilistic, there are things going wrong
         | with the body all the time. Most often this affects a single
         | cell and is corrected by programmed cell death...
        
         | colmmacc wrote:
         | This is how many live-update and hot-patching systems work.
         | 
         | Some changes are easy and reliable; if you need to add a new
         | condition or a few instructions, you can build your new basic
         | block of instructions elsewhere and then atomically insert a
         | jump to that basic block (which then jumps back to the correct
         | post-insertion point).
         | 
         | Others are hard; if you need to add a new variable to some
         | state that's being tracked, then you have to find a way to know
         | when it's a safe time during execution to make that change, and
         | you might have had to wrap accesses to that state in RCU
         | gadgets.
         | 
         | It takes expertise, but it's doable and satisfying when you
         | manage it!
        
       | the5avage wrote:
       | Changing code you don't understand can have effects you did not
       | intend.
       | 
       | Who would have expected that?
        
         | maxerickson wrote:
         | They are more or less exactly describing the change they are
         | making, indicating they do understand the code, they just can't
         | edit it cleanly.
        
           | the5avage wrote:
           | Oh, maybe I missed that we already completely understand how
           | DNA works.
        
             | maxerickson wrote:
             | Yes, we do understand the mutations that we would target
             | with something like crispr, where protein coding has been
             | disrupted by a small error.
        
       | westurner wrote:
       | ScholarlyArticle: "Gene editing of NCF1 loci is associated with
       | homologous recombination and chromosomal rearrangements" (2024)
       | https://www.nature.com/articles/s42003-024-06959-z
        
       | westurner wrote:
       | Does it matter which CRISPR or CRISPR-like method is applied; or
       | is there in general a dynamic response to gene editing in
       | DNA/RNA?
        
         | ca_tech wrote:
         | The article covers this and I think the title is a bit too
         | general. It is a byproduct of how CRISPR works as it targets a
         | specific sequence. In this case the sequence is also present in
         | areas that were non-targeted. Essentially, the sequence was not
         | unique so the process impacted other areas in unintended ways.
        
       | lawrenceyan wrote:
       | We should steer clear of modifying DNA directly until our
       | understanding of biology is much _much_ better.
       | 
       | For now, I think targeting RNA as an intermediate solution is the
       | right approach.
        
         | nharada wrote:
         | I think there are plenty of diseases where people would be
         | willing to roll the dice on low probability unintended
         | consequences if it meant a massive 100% probability life
         | improvement. This research is great because it reduces our
         | uncertainty about the former option.
         | 
         | That said, I wouldn't wanna be the first person to do elective
         | CRISPR therapy for something that I don't actually need (i.e.
         | LASIK, etc).
        
         | thfuran wrote:
         | Somatic cell modification is relatively safe. Or rather, not
         | existentially dangerous to the species unless both extremely
         | widespread and extremely deleterious.
        
         | Nasrudith wrote:
         | How are we to learn how biology works better without modifying
         | DNA directly? We learn through experimentation, not sitting
         | upon a pedestal and pontificating for decades.
        
       | impish9208 wrote:
       | In mice?
        
       | Terr_ wrote:
       | I see a whole bunch of comments here where people have
       | misunderstood the issue.
       | 
       | The problem here is _not_ that unanticipated outcomes arose from
       | our _intended_ fix.
       | 
       | The problem that the exact edit we planned _isn 't happening in
       | the first place_, because the search-replace tools aren't yet
       | specific and reliable enough.
        
         | function_seven wrote:
         | The genetic version of the Clbuttic Mistake?
         | 
         | https://thedailywtf.com/articles/The-Clbuttic-Mistake-
        
         | dmvdoug wrote:
         | This is also not quite accurate. The edit is happening, but the
         | problem is the same word appears three times in the same
         | sentence, and the program can't distinguish them.
         | 
         | Specifically, there are three copies of the gene, the active
         | one and two inactive ones. Trying to only edit one, they ended
         | up hitting ay least one of the others as well. That then caused
         | misalignment and other issues for the rest of the neighborhood.
        
         | maxerickson wrote:
         | It's both. With 2 or 3 cuts, you have several pieces of DNA
         | that recombine in whatever arrangement. So in addition to the
         | disease not being treated, you have other issues.
         | 
         |  _When the sections are subsequently rejoined, entire gene
         | segments may be misaligned or missing. The medical consequences
         | are unpredictable and, in the worst case, contribute to the
         | development of leukemia._
        
       | m3kw9 wrote:
       | We do this because reversing what caused the defect is way out of
       | our league, just like how most advanced drugs work. The point is
       | you take it anyway because you likely have 2 choice.
        
         | maxerickson wrote:
         | They have a targeted DNA edit that will fix the defect. They
         | can't apply it cleanly.
         | 
         | Reversing the cause would require something nonsensical like
         | editing their ancestor's DNA before they were born.
        
       | MillironX wrote:
       | I once got into a debate with a classmate in undergrad. He had
       | seen a Ted Talk and was very worried that CRISPR was going to
       | create a new race of designer babies. I tried to explain that
       | even CRISPR wasn't there yet, but he was under the common
       | misconception that CRISPR is just a text editor for the genome
       | [1].
       | 
       | If we want to take the computer code analogy, CRISPR is not
       | vim/emacs/nano/ect., it is sed -i 's///g' with greedy options on.
       | 
       | The 'g' option is what got the researchers here. I hypothesize
       | that a future problem will be CRISPR targeting previous CRISPR
       | edits since the targets are relatively conserved.
       | 
       | [1]: https://xkcd.com/1823/
        
       | mmcclure wrote:
       | A lot of the graphics that explain how CRISPR work show this very
       | careful snipping of a strand of DNA. Tiny little scissors making
       | pinpoint accuracy revisions. I think that's lead to a deep
       | misunderstanding for most people (including myself) on how this
       | technology actually works.
       | 
       | CRISPR is amazing, but it's still a fairly blunt tool. The
       | article talks about one way: guide RNA can often bind to
       | sequences that are very similar to the intended sequence, but not
       | exactly, meaning it's probable that for every intended cut you're
       | making several unintended ones. The "scissor" action itself, Cas9
       | protein, is less like a scissor cut and more like a jagged tear,
       | which can damage surrounding DNA.
       | 
       | The repair pathways themselves are also imperfect. It's not a
       | copy/paste like infographics show, it's more like emergency duct
       | taping broken ends together.
       | 
       | All of that stuff combined...Again, amazing technology, but I get
       | extremely nervous when I hear people talk about introducing
       | CRISPR-based gene editing into the human gene pool. The
       | generational effects there are still entirely unpredictable at
       | this stage, could be disastrous, and any actual paths to trying
       | to roll things back would be deeply ethically fraught.
        
         | aliasxneo wrote:
         | > the generational effects there are still entirely
         | unpredictable at this stage
         | 
         | Something I've always wondered about CRISPR. It seems the legal
         | case for introducing it is the freedom to perform "body
         | hacking" on yourself. But, at least in this case, isn't it more
         | like "generational hacking?" Maybe I am fundamentally
         | misunderstanding the technology, but it's strange to think
         | about what sort of protections should be put in place to
         | prevent someone being born with severe defects due to messing
         | with the genome.
        
           | dghlsakjg wrote:
           | I'm not sure about that...
           | 
           | Isn't restricting people from reproducing based on their
           | genetic material known as Eugenics?
        
             | mmcclure wrote:
             | This is the "ethically fraught" bit I was referencing. Once
             | this genie is out of the bottle and into the gene pool,
             | there's effectively no moral/ethical path to putting it
             | back in.
        
             | aliasxneo wrote:
             | This certainly highlights the problem. For context, I
             | wasn't suggesting eugenics, although I suppose that's one
             | way to enforce things (one I would never support, anyways).
        
         | jpalawaga wrote:
         | People like to compare CRISPR as scissors or cut/copy-and-
         | replace, but people should think of it more as 'find and
         | replace all'.
         | 
         | in that context, it's much more understandable why the tool has
         | drawbacks.
        
           | mmcclure wrote:
           | Yeah, better analogy, but still a little flawed because that
           | still makes it seem much better/precise than it is. It's
           | "find and replace all" that might:
           | 
           | - occasionally match very similar, but not exact text
           | 
           | - will often subtly alter the text around the replacement
           | area, either by deleting characters or altering others.
        
             | albertgoeswoof wrote:
             | It's more like pasting your genome into chatgpt and asking
             | it to fix it
        
       | ch1kkenm4ss4 wrote:
       | No shit.
       | 
       | I would personally love to get a gene theraphy for an inherited
       | auto-immune disease, but mankind just doesn't have 'the full
       | picture' - yet. So i'll stick with known treatments.
        
       | jayyhu wrote:
       | Consider a scenario where you're editing a function:
       | function foo() { return a*2.1^2+0.52/2 }
       | 
       | So you do a find-all regex "1.*5" and delete _all_ matching
       | occurrences (a la CRISPER) to get:                 function foo()
       | { return a*2.2/2 }
       | 
       | But unbeknownst to you, the code is littered with a bunch of
       | commented out versions of the same function you're trying to
       | edit:                 /* function foo() { return a*1.5/2.1 } */
       | /* function foo() { return a*1.95/2.4 } */
       | 
       | And now those commented out versions now become:
       | /* function foo() { return a*/2.1 } */       /* function foo() {
       | return a*/2.4 } */
       | 
       | And now the whole program doesn't compile anymore--or your
       | patients get Leukemia. Oops.
        
         | kps wrote:
         | You can't parse DNA with regex1.
         | 
         | 1 https://stackoverflow.com/questions/1732348/regex-match-
         | open...
        
           | abc_lisper wrote:
           | Excellent point. But it works for bacteria I guess, because
           | viral dna is small.
        
       | zackmorris wrote:
       | I upvoted this because it's perhaps the most important research
       | being conducted currently. But the seriousness of the issue is
       | misleading.
       | 
       | CRISPR is revolutionary technology. Any side effects of its use
       | require evolutionary improvements. The two are not the same.
       | 
       | With the decades of experience we have dealing with code and
       | information, as well as the arrival of AI, I wish that people
       | would stop obsessing about the difficulty of solving problems.
       | The difficulty is gone. All problems are solvable now, it's just
       | a matter of time, effort, and a tiny fraction of the money that
       | used to be required.
       | 
       | But FUD seems to dominate these discussions. That's probably my
       | biggest disappointment with, say, the rich and powerful who
       | gatekeep funding and the media. It's even easier for them to
       | solve these problems, or encourage healthy debate. But they seem
       | to go out of their way to do the opposite. Like, if it weren't
       | for wealth inequality, we could have been working on this stuff,
       | and found the answers potentially years ago. I'll just never
       | understand the so-called realists and how they hold us back in
       | these times out of fear, which leads to false equivalence and
       | generalization.
        
       | DidYaWipe wrote:
       | I wonder if there's a pattern to genes that are adjacent to the
       | target ones, which is not typically found adjacent to the pseudo
       | ones. In other words, can the "search term" be expanded to make
       | it more selective and then take action on the target region
       | within it.
        
       | kylehotchkiss wrote:
       | Of course editing genes with CRISPR can introduce other defects!
       | Genetic sequences can serve multiple purposes, alternative
       | splicing, polygenic traits etc. It's an exciting discovery with
       | interesting repurpose applications but DNAs application is not
       | just a linear read
        
       | Dwedit wrote:
       | There were some numbnuts that were calling themselves "Bio
       | Hackers" and freely injecting themselves with random CRISPR
       | injections. I wonder what's going to happen to them.
        
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