[HN Gopher] Pharmacokinetics: Drug development's broken stair
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       Pharmacokinetics: Drug development's broken stair
        
       Author : Ariarule
       Score  : 52 points
       Date   : 2023-09-30 19:26 UTC (3 hours ago)
        
 (HTM) web link (trevorklee.substack.com)
 (TXT) w3m dump (trevorklee.substack.com)
        
       | gumby wrote:
       | Yes, pharma is empirical, not predictive. We are very far from
       | understanding biology well enough to be predictive (except on
       | TV).
       | 
       | Look are Loewe's recent column in Science: Target-based drug
       | programs seem like an obviously sensible approach but in practice
       | have not been fruitful: https://www.science.org/content/blog-
       | post/target-based-drug-...
       | 
       | Biology is still art and luck.
       | 
       | Note: I'm a former small molecule pharma developer myself.
        
         | snitty wrote:
         | >We are very far from understanding biology well enough to be
         | predictive (except on TV)
         | 
         | I'm very excited for the next season of Small Drug Discovery on
         | NBC. I hear the first 5 episodes this season are just screening
         | candidates.
        
           | foota wrote:
           | I think the finale will cover a phase 1 trial!
        
         | User23 wrote:
         | One of the most wildly productive periods in small molecule
         | drug discovery was back when crazy, mostly German, chemists
         | would taste their products as part of characterizing them.
         | 
         | That's why, among other things, we have such wonderfully high
         | quality data on progressive mercury poisoning.
        
           | gumby wrote:
           | Saccharin was discovered when Ramsen rolled a cigarette and
           | noticed that the paper tasted sweet (there is a non-tobacco
           | version of this for the faint of heart).
           | 
           | And Alexander Fleming discovered penicillin because some
           | bread from an old sandwich did not become moldy.
           | 
           | Modern lab procedures preclude any such discovery today.
        
       | vonnik wrote:
       | > We could fix this stair. It would just require the raw data
       | from a variety of pharmacokinetic trials, some in-depth
       | experiments on human liver and gastric membranes, and some
       | simulation of the physics of how different drugs diffuse into the
       | bloodstream and across membranes.
       | 
       | This statement seems overly optimistic. Predictive
       | Pharmacokinetics that obviates most trials would need to model
       | all possible drugs for all people. The computational complexity
       | of that problem seems out of reach. The best way to get to know
       | complex adaptive systems (which can't be properly simulated most
       | of the time) is to test them empirically.
        
       | NicotineFiend wrote:
       | I'm surprised the article didn't mention anything about
       | pharmacogenetics. For example, drug-metabolizing enzyme
       | polymorphisms can often lead to a 10+ fold difference in Cmax (or
       | name the parameter) between a poor and an ultrarapid metabolizer
       | of some enzyme.
        
         | klevertree wrote:
         | Author here. Enzyme polymorphisms are tricky and would require
         | a whole different blog post. Some drugs they matter a lot for,
         | some drugs they do not. I actually have not found any drugs
         | with 10-fold variability that could be ascribed solely (or even
         | mainly) to polymorphisms, although it doesn't seem impossible.
        
           | opportune wrote:
           | https://www.ncbi.nlm.nih.gov/books/NBK84174/
           | 
           | Here's an article I found in 30s of searching (granted, I
           | already knew Warfarin was hugely affected by CYP2D6) stating
           | that equivalent maintenance doses of Warfarin can vary by a
           | factor of >10 (from 0.5mg to 7mg) based on the CYP2D6
           | phenotype of the patient.
        
         | 303uru wrote:
         | What drug has a 10 fold difference in Cmax, as a pharmacist I
         | can't think of anything even close to that.
        
           | opportune wrote:
           | Warfarin is one of the most well known scientifically, but as
           | a practitioner you may not know this because hospitals and
           | insurers are scared to acknowledge the ongoing rate of
           | preventable bad outcomes caused by _not_ accounting for
           | variances in metabolism.
           | 
           | That is to say, if we were to actually start assessing
           | patients' ability to metabolize warfarin we'd have to
           | confront the fact that a huge number of bad clinical outcomes
           | in the recent past stemmed from not doing this.
        
             | carbocation wrote:
             | > _hospitals and insurers are scared to acknowledge the
             | ongoing rate of preventable bad outcomes caused by not
             | accounting for variances in metabolism._
             | 
             | Healthcare systems are so aware of and open about
             | warfarin's risks that they have warfarin clinics set up to
             | repeatedly measure patients' prothrombin times so that they
             | can adjust dosing empirically. Further, they also provide
             | nutritional guidance to patients taking warfarin to help
             | them reduce diet-influenced variance in warfarin
             | metabolism.
        
           | scheme271 wrote:
           | What about codeine with ultra-rapid metabolizers (e.g. the
           | significant population in Saudi Arabia), it might not be a
           | 10x difference but normal dosages can result in overdose or
           | death in people that are ultra-rapid metabolizers or even in
           | their babies if they are nursing mothers.
        
           | NicotineFiend wrote:
           | Many tricyclic antidepressants metabolized by CYP2D6 would be
           | here, if you put the nonmetabolizers up against the rapid
           | metabolizer, https://en.wikipedia.org/wiki/Doxepin for
           | example.
        
           | klevertree wrote:
           | Cyclosporine and tacrolimus, if you look at the range in any
           | of their pk trials you'll easily see 10 fold variability.
        
       | marcosfelt wrote:
       | There's a company called VeriSIM life trying to make the
       | physiological models mentioned in the post more accessible [1].
       | They apparently fit their models across a bunch of publicly
       | available and proprietary data. I found some peer-reviewed
       | publications (e.g. [2]), but I am not sure how widely they are
       | used.
       | 
       | [1] https://www.verisimlife.com/our-platform [2]
       | https://www.tandfonline.com/doi/full/10.2147/DDDT.S253064?ro...
        
         | cowsandmilk wrote:
         | Simulations Plus has been building models on this data since
         | 1996 and is one of the more popular vendors for prebuilt
         | software for this modeling. There's literally dozens of vendors
         | with software though because companies have been working on
         | this since the 80's despite the article's claim that this has
         | been an ignored problem.
         | 
         | https://en.m.wikipedia.org/wiki/Simulations_Plus
        
       | jrflowers wrote:
       | I like how the author has discovered that a problem that costs
       | pharma companies billions of dollars actually has a quick fix:
       | simply model how livers react to infinite compounds.
       | 
       | Since all livers behave the same and there is no variation based
       | on gene expression or disease, this is a trivial task! The reason
       | why this hasn't been Solved is because none have been Disruptive
       | enough to dream of doing research in this area.
        
         | radus wrote:
         | Moreover, pharma companies and academics already do model PK..
         | it's a huge field of study, not some ignored "broken stair" -
         | there is definitely "serious money" behind this.
        
         | klevertree wrote:
         | Author here. That's not what I said. Please don't be a jerk on
         | the Internet.
        
           | jrflowers wrote:
           | You literally wrote
           | 
           | > It would just require the raw data from a variety of
           | pharmacokinetic trials, some in-depth experiments on human
           | liver and gastric membranes, and some simulation of the
           | physics of how different drugs diffuse into the bloodstream
           | and across membranes. This would be difficult, but not
           | impossible, and would not require any huge scientific
           | advances.
        
       | cowsandmilk wrote:
       | As someone who has worked in pharma, this article is pretty damn
       | ignorant. There's a ton of funding for pharmacokinetics work. For
       | liver and the gut, it is widely agreed that 2-D tissue culture is
       | completely non-predictive, so the last couple of decades have
       | been building 3-D tissue culture and nowadays, companies
       | commercially purchase organs on a chip for both and even multi-
       | organ systems[0]. Plenty of companies have internal teams that
       | have built similar technology and they all have teams working
       | hard trying to build computational models on the generated data.
       | But small changes in molecules have huge ADMET impacts and these
       | organs are just a subset of the organs that can impact
       | pharmacokinetics. Plus, toxicology can tank a drug by impacts on
       | nearly any organ, so whole animal models always still win.
       | 
       | The entire article just yells ignorance of what drug companies
       | work on and what they're investing in.
       | 
       | [0] https://cn-bio.com/models/
        
         | klevertree wrote:
         | Author here. As someone who works in pharma, organ on a chip
         | models are not even close to being relevant to providing
         | accurate PK curves for oral absorption. The state of the art is
         | trying to make it work for cutaneous absorption and that's
         | still not great/commercially useful.
         | 
         | My whole point is that there needs to be way more open data on
         | pharmacokinetics. That's the only way we're going to solve
         | this.
        
       | snitty wrote:
       | This is very interesting, and I think massively underestimates
       | the variability in how small molecular drugs are affected by the
       | body. Small differences in molecules can have drastic effects on
       | where, how, and how quickly they're adsorbed, and what systems
       | they affect.
       | 
       | More than anything, I think this just underestimates the
       | unpredictability of it all. To extend the author's metaphor, if
       | you measure the 100 data points from shooting 10 different
       | projectiles out of 10 different devices, on 10 different
       | celestial bodies, you're still not going to have a lot of
       | predictive power that can be generalized.
        
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       (page generated 2023-09-30 23:00 UTC)